Access the full text.
Sign up today, get DeepDyve free for 14 days.
Loading next page...
/lp/wiley/longitudinal-data-analysis-repeated-measures-in-clinical-trials-0llDm0qSpi
References (136)
-
P. Heagerty, S. Zeger (1998)
Lorelogram: A Regression Approach to Exploring Dependence in Longitudinal Categorical ResponsesJournal of the American Statistical Association, 93
-
L. Wei, J. Lachin (1984)
Two-Sample Asymptotically Distribution-Free Tests for Incomplete Multivariate ObservationsJournal of the American Statistical Association, 79
-
Laird Laird, Donnelly Donnelly, Ware Ware (1992)
Longitudinal studies with continuous responsesStatistical Methods in Medical Research, 1
-
R. Cook, E. Ng (1997)
A logistic-bivariate normal model for overdispersed two-state Markov processes.Biometrics, 53 1
-
D. Geary (1988)
Sequential testing in clinical trials with repeated measurementsBiometrika, 75
-
Albert Albert, Brown Brown (1991)
The design of a panel study under an alternating Poisson assumptionBiometrics, 47
-
Richard Cook, J. Lawless (1996)
Interim monitoring of longitudinal comparative studies with recurrent event responses.Biometrics, 52 4
-
M. Lindstrom, D. Bates (1990)
Nonlinear mixed effects models for repeated measures data.Biometrics, 46 3
-
M. Espeland, O. Platt, D. Gallagher (1989)
Joint Estimation of Incidence and Diagnostic Error Rates from Irregular Longitudinal DataJournal of the American Statistical Association, 84
-
K. Lan, D. Zucker (1993)
Sequential monitoring of clinical trials: the role of information and Brownian motion.Statistics in medicine, 12 8
-
A. Stuart, D. Cox (1971)
The analysis of binary data, 134
-
D. Follmann, D. Lambert (1989)
Generalizing Logistic Regression by Nonparametric MixingJournal of the American Statistical Association, 84
-
M. Lindstrom, D. Bates (1988)
Newton-Raphson and EM Algorithms for Linear Mixed-Effects Models for Repeated-Measures DataJournal of the American Statistical Association, 83
-
S. Zeger, K. Liang (1986)
Longitudinal data analysis for discrete and continuous outcomes.Biometrics, 42 1
-
Christopher Morrell, J. Pearson, H. Carter, Larry Brant (1995)
Estimating Unknown Transition Times Using a Piecewise Nonlinear Mixed-Effects Model in Men with Prostate CancerJournal of the American Statistical Association, 90
-
Margaret Wu, Kent Bailey (1989)
Estimation and comparison of changes in the presence of informative right censoring: conditional linear model.Biometrics, 45 3
-
P. Heagerty, S. Zeger (1996)
Marginal Regression Models for Clustered Ordinal MeasurementsJournal of the American Statistical Association, 91
-
P. Albert, S. Hunsberger, F. Biro (1997)
Modeling Repeated Measures with Monotonic Ordinal Responses and Misclassification, with Applications to Studying MaturationJournal of the American Statistical Association, 92
-
J. Neuhaus (1992)
Statistical methods for longitudinal and clustered designs with binary responsesStatistical Methods in Medical Research, 1
-
Lee-Jen Wei, Wayne Johnson (1985)
Combining dependent tests with incomplete repeated measurementsBiometrika, 72
-
E. Vonesh, R. Carter (1992)
Mixed-effects nonlinear regression for unbalanced repeated measures.Biometrics, 48 1
-
J. Lang, A. Agresti (1994)
Simultaneously Modeling Joint and Marginal Distributions of Multivariate Categorical ResponsesJournal of the American Statistical Association, 89
-
Richard Jones (1994)
Longitudinal Data with Serial Correlation : A State-Space ApproachTechnometrics, 36
-
N. Laird, J. Ware (1982)
Random-effects models for longitudinal data.Biometrics, 38 4
-
Calyampudi Rao (1959)
SOME PROBLEMS INVOLVING LINEAR HYPOTHESES IN MULTIVARIATE ANALYSISBiometrika, 46
-
K. Liang, S. Zeger, B. Qaqish (1992)
Multivariate Regression Analyses for Categorical DataJournal of the royal statistical society series b-methodological, 54
-
Edward Vonesh, Vernon Chinchilli, Kewei Pu (1996)
Goodness-of-fit in generalized nonlinear mixed-effects models.Biometrics, 52 2
-
R. Mcmahon, M. Waclawiw, N. Geller, F. Barton, M. Terrin, D. Bonds (1997)
An extension of stochastic curtailment for incompletely reported and classified recurrent events: the Multicenter Study of Hydroxyurea in Sickle Cell Anemia (MSH).Controlled clinical trials, 18 5
-
K. Lan, David Detlets, M. Halperin (1984)
More flexible sequential and non-sequential designs in long-term clinical trialCommunications in Statistics-theory and Methods, 13
-
Podgor Podgor, Hiller Hiller (1996)
Associations of types of lens opacities between and within eyes of individuals: An application of second‐order generalized estimating equationsStatistics in Medicine, 15
-
J. Rochon (1995)
Supplementing the Intent-to-Treat Analysis: Accounting for Covariates Observed Postrandomization in Clinical TrialsJournal of the American Statistical Association, 90
-
M. Podgor, R. Hiller (1996)
Associations of types of lens opacities between and within eyes of individuals: an application of second-order generalized estimating equations. The Framingham Eye Studies Group.Statistics in medicine, 15 2
-
S. Gange, D. DeMets (1996)
Sequential monitoring of clinical trials with correlated responsesBiometrika, 83
-
J. Lawless (1987)
Regression Methods for Poisson Process DataJournal of the American Statistical Association, 82
-
Rolley Johnson, J. Jaffe, P. Fudala (1992)
A controlled trial of buprenorphine treatment for opioid dependence.JAMA, 267 20
-
P. Albert, D. Follmann, H. Barnhart (1997)
A generalized estimating equation approach for modeling random length binary vector data.Biometrics, 53 3
-
Liang Liang, Zeger Zeger, Qaqish Qaqish (1992)
Multivariate regression analyses for categorical data (with discussion)Journal of the Royal Statistical Society, Series B, 54
-
Muenz Muenz, Rubinstein Rubinstein (1985)
Markov models for covariate dependence of binary sequenceBiometrics, 43
-
R. Cook, J. Lawless, Claude Nadeau (1996)
Robust tests for treatment comparisons based on recurrent event responses.Biometrics, 52 2
-
Margaret Wu, R. Carroll (1988)
Estimation and comparison of changes in the presence of informative right censoring by modeling the censoring processBiometrics, 44
-
L. Wei, D. Lin, L. Weissfeld (1989)
Regression analysis of multivariate incomplete failure time data by modeling marginal distributionsJournal of the American Statistical Association, 84
-
R. Prentice (1988)
Correlated binary regression with covariates specific to each binary observation.Biometrics, 44 4
-
R. Potthoff, S. Roy (1964)
A generalized multivariate analysis of variance model useful especially for growth curve problemsBiometrika, 51
-
S. Zeger, B. Qaqish (1988)
Markov regression models for time series: a quasi-likelihood approach.Biometrics, 44 4
-
Dietary Intervention Study in Children (DISC) with elevated low‐density‐lipoprotein cholesterol. Design and baseline characteristics
Annals of Epidemiology, 3
-
E. Slud, L. Wei (1982)
Two-Sample Repeated Significance Tests Based on the Modified Wilcoxon StatisticJournal of the American Statistical Association, 77
-
C. Frost, R. Clarke, H. Beacon (1999)
Use of hierarchical models for meta-analysis: experience in the metabolic ward studies of diet and blood cholesterol.Statistics in medicine, 18 13
-
J. Ware (1985)
Linear Models for the Analysis of Longitudinal StudiesThe American Statistician, 39
-
K. Lan, D. DeMets (1983)
Discrete sequential boundaries for clinical trialsBiometrika, 70
-
N. Laird, C. Donnelly, J. Ware (1992)
Review papers : Longitudinal studies with continuous responsesStatistical Methods in Medical Research, 1
-
L. Wei, John Su, J. Lachin (1990)
Interim analyses with repeated measurements in a sequential clinical trialBiometrika, 77
-
Stasny Stasny (1987)
Some Markov‐chain models for nonresponse in estimating gross labor force flowsJournal of Official Statistics, 3
-
J. Rochon (1996)
Accounting for Covariates Observed Post Randomization for Discrete and Continuous Repeated Measures DataJournal of the royal statistical society series b-methodological, 58
-
P. Diggle, P.J. Heagerty, Kung Liang, S. Zeger (1994)
Analysis of longitudinal data -
E. Rodin (1985)
Temporal lobe epilepsy and the Bear‐Fedio personality inventoryNeurology, 35
-
C. Waternaux, N. Laird, J. Ware (1989)
Methods for Analysis of Longitudinal Data: Blood-Lead Concentrations and Cognitive DevelopmentJournal of the American Statistical Association, 84
-
K. Liang, S. Zeger (1986)
Longitudinal data analysis using generalized linear modelsBiometrika, 73
-
J. Neuhaus (1993)
Estimation efficiency and tests of covariate effects with clustered binary data.Biometrics, 49 4
-
P. Thall, Stephen Vail (1990)
Some covariance models for longitudinal count data with overdispersion.Biometrics, 46 3
-
H. Barnhart, A. Sampson (1995)
Multiple population models for multivariate random length data--with applications in clinical trials.Biometrics, 51 1
-
M. Halperin, K. Lan, E. Wright, M. Foulkes (1987)
Stochastic curtailing for comparison of slopes in longitudinal studies.Controlled clinical trials, 8 4
-
Peter Thall (1988)
Mixed Poisson likelihood regression models for longitudinal interval count data.Biometrics, 44 1
-
Avital Cnaan, Nan Laird, Peter Slasor (1997)
Using the general linear mixed model to analyse unbalanced repeated measures and longitudinal data.Statistics in medicine, 16 20
-
P. Albert, M. Waclawiw (1998)
A two-state Markov chain for heterogeneous transitional data: a quasi-likelihood approach.Statistics in medicine, 17 13
-
P. Albert, James Dweyer, M. Feinleib, P. Lippert, H. Hoffmeister (1992)
Statistical Models for Longitudinal Studies of Health -
Diggle Diggle, Kenward Kenward (1994)
Informative dropout in longitudinal data analysis (with discussion)Applied Statistics, 43
-
J. Preisser, B. Qaqish (1996)
Deletion diagnostics for generalised estimating equationsBiometrika, 83
-
J. Dawson, S. Lagakos (1993)
Size and power of two-sample tests of repeated measures data.Biometrics, 49 4
-
P. Albert, C. Brown (1991)
The design of a panel study under an alternating Poisson process assumption.Biometrics, 47 3
-
Follmann Follmann, Hunsberger Hunsberger, Albert Albert (1999)
Repeated probit regression when covariates are measured with errorBiometrics
-
C. Davis, L. Wei (1988)
Nonparametric methods for analyzing incomplete nondecreasing repeated measurements.Biometrics, 44 4
-
L. Zhao, R. Prentice (1990)
Correlated binary regression using a quadratic exponential modelBiometrika, 77
-
C. Rao (1958)
Some statistical methods for comparison of growth curves.Biometrics, 14
-
S. Pocock, N. Geller, A. Tsiatis (1987)
The analysis of multiple endpoints in clinical trials.Biometrics, 43 3
-
P. O'Brien, T. Fleming (1979)
A multiple testing procedure for clinical trials.Biometrics, 35 3
-
B. Turnbull, W. Jiang, L. Clark (1997)
Regression models for recurrent event data: parametric random effects models with measurement error.Statistics in medicine, 16 8
-
E. Vonesh, R. Carter (1987)
Efficient inference for random-coefficient growth curve models with unbalanced data.Biometrics, 43 3
-
G. Verbeke, E. Lesaffre (1996)
A Linear Mixed-Effects Model with Heterogeneity in the Random-Effects PopulationJournal of the American Statistical Association, 91
-
S. Zeger, K. Liang, P. Albert (1988)
Models for longitudinal data: a generalized estimating equation approach.Biometrics, 44 4
-
R. Cook (1995)
The design and analysis of randomized trials with recurrent events.Statistics in medicine, 14 19
-
M. Crowder, D. Hand (1990)
Analysis of Repeated Measures -
M. Wu, K. Lan (1992)
Sequential monitoring for comparison of changes in a response variable in clinical studies.Biometrics, 48 3
-
Espeland Espeland, Platt Platt, Gallagher Gallagher (1989)
Joint estimation of incidence and error rates from irregular longitudinal dataJournal of the American Statistical Association, 84
-
G. Liu, K. Liang (1997)
Sample size calculations for studies with correlated observations.Biometrics, 53 3
-
Mark Ashby, J. Neuhaus, W. Hauck, P. Bacchetti, D. Heilbron, N. Jewell, Mark Segal, R. Fusaro (1992)
An annotated bibliography of methods for analysing correlated categorical data.Statistics in medicine, 11 1
-
J. Kalbfleisch, J. Lawless (1985)
The Analysis of Panel Data under a Markov AssumptionJournal of the American Statistical Association, 80
-
V. Gruttola, J. Ware, T. Louis (1987)
Influence Analysis of Generalized Least Squares EstimatorsJournal of the American Statistical Association, 82
-
G. Molenberghs, E. Lesaffre (1994)
Marginal Modeling of Correlated Ordinal Data Using a Multivariate Plackett DistributionJournal of the American Statistical Association, 89
-
S. Pocock (1977)
Group sequential methods in the design and analysis of clinical trialsBiometrika, 64
-
J. Robins, A. Rotnitzky, L. Zhao (1995)
Analysis of semiparametric regression models for repeated outcomes in the presence of missing dataJournal of the American Statistical Association, 90
-
Steven Butler, T. Louis (1992)
Random effects models with non-parametric priors.Statistics in medicine, 11 14-15
-
M. Conaway (1993)
Non-ignorable Non-response Models for Time-ordered Categorical VariablesJournal of The Royal Statistical Society Series C-applied Statistics, 42
-
D. Follmann, Margaret Wu, N. Geller (1994)
testing treatment efficacy in clinical trials with repeated binary measurements and missing observationsCommunications in Statistics-theory and Methods, 23
-
M. Mori, Robert Woolson, George Woodworth (1994)
Slope estimation in the presence of informative right censoring: modeling the number of observations as a geometric random variable.Biometrics, 50 1
-
Calyampudi Rao (1965)
The theory of least squares when the parameters are stochastic and its application to the analysis of growth curves.Biometrika, 52 3
-
Michael Miller, C. Davis, J. Landis (1993)
The analysis of longitudinal polytomous data: generalized estimating equations and connections with weighted least squares.Biometrics, 49 4
-
Molenberghs Molenberghs, Lesaffre Lesaffre (1994)
Marginal modeling of correlated ordinal data using an n‐way Plackett distributionJournal of the American Statistical Association, 89
-
James Lindsey, Philippe Lambert (1998)
On the appropriateness of marginal models for repeated measurements in clinical trials.Statistics in medicine, 17 4
-
M. Kosorok, W. Chao (1996)
The Analysis of Longitudinal Ordinal Response Data in Continuous TimeJournal of the American Statistical Association, 91
-
S. Zeger, M. Karim (1991)
Generalized linear models with random e ects: a Gibbs sampling approach -
G. Fitzmaurice (1995)
A caveat concerning independence estimating equations with multivariate binary data.Biometrics, 51 1
-
M. Lefkopoulou, L. Ryan (1993)
Global tests for multiple binary outcomes.Biometrics, 49 4
-
N. Breslow, D. Clayton (1993)
Approximate inference in generalized linear mixed modelsJournal of the American Statistical Association, 88
-
H. Barnhart, J. Williamson (1998)
Goodness-of-fit tests for GEE modeling with binary responses.Biometrics, 54 2
-
R. Cook, J. Lawless (1997)
Marginal analysis of recurrent events and a terminating event.Statistics in medicine, 16 8
-
L. Fahrmeir, H. Kaufmann (1987)
REGRESSION MODELS FOR NON‐STATIONARY CATEGORICAL TIME SERIESJournal of Time Series Analysis, 8
-
A. Rotnitzky, N. Jewell (1990)
Hypothesis testing of regression parameters in semiparametric generalized linear models for cluster correlated dataBiometrika, 77
-
Leppik Leppik (1985)
A double‐blind crossover evaluation of progabide in partial seizuresNeurology, 35
-
Fitzmaurice Fitzmaurice, Laird Laird (1993)
A likelihood‐based method for analysing longitudinal binary dataBiometrika, 80
-
S. Lipsitz, Kyungeun Kim, L. Zhao (1994)
Analysis of repeated categorical data using generalized estimating equations.Statistics in medicine, 13 11
-
Jae Lee, D. DeMets (1991)
Sequential Comparison of Changes with Repeated Measurements DataJournal of the American Statistical Association, 86
-
L. Kastrukoff, J. Oger, S. Hashimoto, S. Sacks, D. Li, M. Palmér, R. Koopmans, A. Petkau, J. Berkowitz, D. Paty (1990)
Systemic lymphoblastoid interferon therapy in chronic progressive multiple Sclerosis. I. Clinical and MRI evaluationNeurology, 40
-
J. Rochon, R. Helms (1989)
Maximum likelihood estimation for incomplete repeated-measures experiments under an ARMA covariance structure.Biometrics, 45 1
-
H. Goldstein, J. Rasbash (1996)
Improved Approximations for Multilevel Models with Binary ResponsesJournal of The Royal Statistical Society Series A-statistics in Society, 159
-
E. Chi, G. Reinsel (1989)
Models for Longitudinal Data with Random Effects and AR(1) ErrorsJournal of the American Statistical Association, 84
-
R. Stiratelli, N. Laird, J. Ware (1984)
Random-effects models for serial observations with binary response.Biometrics, 40 4
-
R. Omar, E. Wright, R. Turner, S. Thompson (1999)
Analysing repeated measurements data: a practical comparison of methods.Statistics in medicine, 18 13
-
M. Waclawiw, K. Liang (1993)
Prediction of Random Effects in the Generalized Linear ModelJournal of the American Statistical Association, 88
-
M. Palmer (1985)
Clinical Trials: A Practical Approach, 148
-
Zhao Zhao, Prentice Prentice (1990)
Correlated binary regression using a generalized quadratic modelBiometrika, 77
-
A. Rotnitzky, D. Wypij (1994)
A note on the bias of estimators with missing data.Biometrics, 50 4
-
P. McCullagh, J. Nelder (1984)
Generalized Linear Models -
H. Abu-Libdeh, B. Turnbull, L. Clark (1990)
Analysis of multi-type recurrent events in longitudinal studies; application to a skin cancer prevention trial.Biometrics, 46 4
-
N. Lange, L. Ryan (1989)
ASSESSING NORMALITY IN RANDOM EFFECTS MODELSAnnals of Statistics, 17
-
P. Diggle, M. Kenward (1994)
Informative Drop‐Out in Longitudinal Data AnalysisApplied statistics, 43
-
J. Neuhaus, J. Kalbfleisch, W. Hauck (1991)
A Comparison of Cluster-Specific and Population-Averaged Approaches for Analyzing Correlated Binary DataInternational Statistical Review, 59
-
J. Rochon (1992)
ARMA Covariance Structures with Time Heteroscedasticity for Repeated Measures ExperimentsJournal of the American Statistical Association, 87
-
G. Molenberghs, M. Kenward, E. Lesaffre (1997)
The analysis of longitudinal ordinal data with nonrandom drop-outBiometrika, 84
-
Intermittent positive pressure breathing therapy of chronic obstructive pulmonary disease
Annals of Internal Medicine, 99
-
P. Albert (2000)
A Transitional Model for Longitudinal Binary Data Subject to Nonignorable Missing DataBiometrics, 56
-
Paul Albert, Lisa McShane (1995)
A generalized estimating equations approach for spatially correlated binary data: applications to the analysis of neuroimaging data.Biometrics, 51 2
-
G. Fitzmaurice, N. Laird (1993)
A likelihood-based method for analysing longitudinal binary responsesBiometrika, 80
-
D. Follmann, Margaret Wu (1995)
An approximate generalized linear model with random effects for informative missing data.Biometrics, 51 1
-
M. Espeland, J. Rushing, A. Vault (1993)
Estimating incidence and diagnostic error rates for bivariate progressive processes.Biometrics, 49 4
-
Robert Weiss, Carlos Lazaro (1992)
Residual plots for repeated measures.Statistics in medicine, 11 1
-
Harvey Goldstein, Michael Healy, J. Rasbash (1994)
Multilevel time series models with applications to repeated measures data.Statistics in medicine, 13 16
- Publisher
- Wiley
- Copyright
- Published in 1999 by John Wiley & Sons, Ltd. This article is a US Government work and is the public domain in the United States
- ISSN
- 0277-6715
- eISSN
- 1097-0258
- DOI
- 10.1002/(SICI)1097-0258(19990715)18:13<1707::AID-SIM138>3.0.CO;2-H
- Publisher site
- See Article on Publisher Site
Abstract
Longitudinal data is often collected in clinical trials to examine the effect of treatment on the disease process over time. This paper reviews and summarizes much of the methodological research on longitudinal data analysis from the perspective of clinical trials. We discuss methodology for analysing Gaussian and discrete longitudinal data and show how these methods can be applied to clinical trials data. We illustrate these methods with five examples of clinical trials with longitudinal outcomes. We also discuss issues of particular concern in clinical trials including sequential monitoring and adjustments for missing data. A review of current software for analysing longitudinal data is also provided. Published in 1999 by John Wiley & Sons, Ltd. This article is a US Government work and is the public domain in the United States.
Journal
Statistics in Medicine – Wiley
Published: Jul 15, 1999