%0 Journal Article
%T Intravenous administration of scAAV9-Hexb normalizes lifespan and prevents pathology in Sandhoff disease mice
%A Niemir, Natalia
%A Rouvière, Laura
%A Besse, Aurore
%A Vanier, Marie T
%A Dmytrus, Jasmin
%A Marais, Thibaut
%A Astord, Stéphanie
%A Puech, Jean-Philippe
%A Panasyuk, Ganna
%A Cooper, Jonathan D
%A Barkats, Martine
%A Caillaud, Catherine
%J Human Molecular Genetics
%V 27
%N 6
%P 954-968
%@ 0964-6906
%D 2018-01-08
%I Oxford University Press
%~ DeepDyve