%0 Journal Article %T Clinical and preclinical therapeutic outcome metrics for USH2A-related disease %A Toms, Maria %A Dubis, Adam M %A de Vrieze, Erik %A Tracey-White, Dhani %A Mitsios, Andreas %A Hayes, Matthew %A Broekman, Sanne %A Baxendale, Sarah %A Utoomprurkporn, Nattawan %A Bamiou, Doris %A Bitner-Glindzicz, Maria %A Webster, Andrew R %A Van Wijk, Erwin %A Moosajee, Mariya %J Human Molecular Genetics %V 29 %N 11 %P 1882-1899 %@ 0964-6906 %D 2020-07-21 %I Oxford University Press %~ DeepDyve