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References (7)
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Thiago Cabral, James DiCarlo, Sally Justus, Jesse Sengillo, Yu Xu, S. Tsang (2017)
CRISPR applications in ophthalmologic genome surgeryCurrent Opinion in Ophthalmology, 28
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Trinucleotide Repeat Expansion in the Transcription Factor 4 (TCF4) Gene Leads to Widespread mRNA Splicing Changes in Fuchs' Endothelial Corneal DystrophyInvestigative Ophthalmology & Visual Science, 58
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C. Dunbar, K. High, J. Joung, D. Kohn, K. Ozawa, M. Sadelain (2018)
Gene therapy comes of ageScience, 359
- Publisher
- American Medical Association
- Copyright
- Copyright 2018 American Medical Association. All Rights Reserved.
- ISSN
- 2168-6165
- eISSN
- 2168-6173
- DOI
- 10.1001/jamaophthalmol.2018.2324
- Publisher site
- See Article on Publisher Site
Abstract
This Viewpoint explains the possibility of clustered regularly interspaced short palindromic repeats (CRISPR) gene editing becoming a means of treating Fuchs endothelial corneal dystrophy.
Journal
JAMA Ophthalmology – American Medical Association
Published: Sep 21, 2018